Hughes, M., Smith, D., Morris, L., Fletcher, C., Colaco, A., Huebecker, M., . . . Rahim, A. (2018). AAV9 intracerebroventricular gene therapy improves lifespan, locomotor function and pathology in a mouse model of Niemann-Pick type C1 disease. Oxford University Press.

Hughes, MP, et al. AAV9 Intracerebroventricular Gene Therapy Improves Lifespan, Locomotor Function and Pathology in a Mouse Model of Niemann-Pick Type C1 Disease. Oxford University Press, 2018.

Hughes, MP, et al. AAV9 Intracerebroventricular Gene Therapy Improves Lifespan, Locomotor Function and Pathology in a Mouse Model of Niemann-Pick Type C1 Disease. Oxford University Press, 2018.