Preclinical development of antisense conjugates for the treatment of myotonic dystrophy 1

<p>Myotonic dystrophy type 1 (DM1) is a complex autosomal dominant neuromuscular disorder that affects approximately 1 in 8,000 individuals. DM1 impacts multiple organ systems, including skeletal muscle, heart and central nervous system (CNS), leading to a diverse range of symptoms. Despite on...

Бүрэн тодорхойлолт

Номзүйн дэлгэрэнгүй
Үндсэн зохиолч: Stoodley, J
Бусад зохиолчид: Varela-Muino, M
Формат: Дипломын ажил
Хэл сонгох:English
Хэвлэсэн: 2024
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