Genetic medicines for CF: Hype versus reality

Genetic medicines for CF: Hype versus reality

Since identification of the CFTR gene over 25 years ago, gene therapy for cystic fibrosis (CF) has been actively developed. More recently gene therapy has been joined by other forms of "genetic medicines" including mRNA delivery, as well as genome editing and mRNA repair-based strategies....

Detaylı Bibliyografya
Asıl Yazarlar:	Alton, E, Boyd, A, Davies, J, Gill, D, Griesenbach, U, Harrison, P, Henig, N, Higgins, T, Hyde, S, Innes, J, Korman, M
Materyal Türü:	Journal article
Dil:	English
Baskı/Yayın Bilgisi:	Wiley 2016

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