Beneficial effects on vision in patients undergoing retinal gene therapy for choroideremia
Retinal gene therapy is increasingly recognized as a novel molecular intervention that has huge potential in treating common causes of blindness, the majority of which have a genetic aetiology1,2,3,4,5. Choroideremia is a chronic X-linked retinal degeneration that was first described in 18726. It le...
Main Authors: | Xue, K, Jolly, J, Barnard, A, Rudenko, A, Salvetti, A, Patrício, M, Edwards, T, Groppe, M, Orlans, H, Tolmachova, T, Black, G, Webster, A, Lotery, A, Holder, G, Downes, S, Seabra, M, MacLaren, R |
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Format: | Journal article |
Published: |
Springer Nature
2018
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