New treatments in spinal muscular atrophy: an overview of currently available data
<p><strong>Introduction:</strong> Spinal muscular atrophy (SMA) is one of the most common inherited neuromuscular disorders. It causes progressive muscle weakness and results in significant disability. Until recently, there were no drugs available for the treatment of SMA. Several...
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| Format: | Journal article |
| Langue: | English |
| Publié: |
Taylor and Francis
2020
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