Nusinersen in patients older than 7 months with spinal muscular atrophy type 1: A cohort study

Nusinersen in patients older than 7 months with spinal muscular atrophy type 1: A cohort study

<p><strong>Objective</strong> To evaluate the safety and clinical efficacy of nusinersen in patients older than 7 months with spinal muscular atrophy type 1 (SMA1). <p><strong>Methods</strong> Patients with SMA1 were treated with nusinersen by intrathecal injecti...

Bibliografiset tiedot
Päätekijät:	Aragon-Gawinska, K, Seferian, AM, Daron, A, Gargaun, E, Vuillerot, C, Cances, C, Ropars, J, Chouchane, M, Cuppen, I, Hughes, I, Illingworth, M, Marini-Bettolo, C, Rambaud, J, Taytard, J, Annoussamy, M, Scoto, M, Gidaro, T, Servais, LJP
Aineistotyyppi:	Journal article
Kieli:	English
Julkaistu:	Wolters Kluwer Health, Inc. on behalf of the American Academy of Neurology 2018

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