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  • AAV-U7snRNA mediated multi exo...
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AAV-U7snRNA mediated multi exon-skipping for Duchenne muscular dystrophy

AAV-U7snRNA mediated multi exon-skipping for Duchenne muscular dystrophy

Čájet eará veršuvnnaid (1)
Bibliográfalaš dieđut
Váldodahkkit: Goyenvalle, A, Babbs, A, Garcia, L, Davies, K
Materiálatiipa: Conference item
Almmustuhtton: 2010
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  • AAV-U7snRNA mediated multi exon-skipping for Duchenne muscular dystrophy
    Dahkki: Goyenvalle, A, et al.
    Almmustuhtton: (2011)
  • Engineering exon-skipping vectors expressing U7 snRNA constructs for Duchenne muscular dystrophy gene therapy.
    Dahkki: Goyenvalle, A, et al.
    Almmustuhtton: (2011)
  • Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy
    Dahkki: Goyenvalle, A, et al.
    Almmustuhtton: (2012)
  • Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy.
    Dahkki: Goyenvalle, A, et al.
    Almmustuhtton: (2012)
  • Upgrading U7snRNA To Complete Efficient Rescue of Dystrophin by Exon-Skipping in DMD Patients
    Dahkki: Goyenvalle, A, et al.
    Almmustuhtton: (2009)

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