Gene therapy for retinal dystrophies
Genetic mutations are the cause of inherited retinal dystrophies. The underlying genetic basis of these diseases suggests that a gene therapy approach is logical either to replace or reduce the expression of defective genes. The first proof-of-concept clinical studies in patients with Leber's c...
| Hauptverfasser: | , , |
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| Format: | Journal article |
| Sprache: | German |
| Veröffentlicht: |
2012
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