Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy

Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy

Hiển thị phiên bản (1) khác

Duchenne muscular dystrophy (DMD) is a fatal muscle wasting disorder caused by mutations in the dystrophin gene. Antisense-mediated exon skipping is one of the most promising approaches for the treatment of DMD but still faces personalized medicine challenges as different mutations found in DMD pati...

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Những tác giả chính:	Goyenvalle, A, Wright, J, Babbs, A, Wilkins, V, Garcia, L, Davies, K
Định dạng:	Journal article
Ngôn ngữ:	English
Được phát hành:	2012

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