Strategies to facilitate the long-term expression of transgenes for treatment of chronic liver disease
<p>The development of new gene therapy products offers ground-breaking opportunities for the treatment of human disease. To provide lasting benefit to patients, the expression of a correct copy of a non-functional gene needs to be life-long, and the maintenance of therapeutic levels of gene ex...
Main Author: | van Haasteren, J |
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Other Authors: | Gill, D |
Format: | Thesis |
Published: |
2019
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Subjects: |
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