Surrogate gene therapy for muscular dystrophy
An engineered truncated gene derived from the dystrophin-related protein (utrophin), prevents pathology without an immune response in an animal model of Duchenne muscular dystrophy (DMD) gene therapy.
| Κύριοι συγγραφείς: | , |
|---|---|
| Μορφή: | Journal article |
| Γλώσσα: | English |
| Έκδοση: |
Springer Nature
2019
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| _version_ | 1826285417286074368 |
|---|---|
| author | Davies, KE Chamberlain, JS |
| author_facet | Davies, KE Chamberlain, JS |
| author_sort | Davies, KE |
| collection | OXFORD |
| description | An engineered truncated gene derived from the dystrophin-related protein (utrophin), prevents pathology without an immune response in an animal model of Duchenne muscular dystrophy (DMD) gene therapy. |
| first_indexed | 2024-03-07T01:28:31Z |
| format | Journal article |
| id | oxford-uuid:92c93d21-c69b-4c06-9d3c-8b72e0aa5a05 |
| institution | University of Oxford |
| language | English |
| last_indexed | 2024-03-07T01:28:31Z |
| publishDate | 2019 |
| publisher | Springer Nature |
| record_format | dspace |
| spelling | oxford-uuid:92c93d21-c69b-4c06-9d3c-8b72e0aa5a052022-03-26T23:28:01ZSurrogate gene therapy for muscular dystrophyJournal articlehttp://purl.org/coar/resource_type/c_dcae04bcuuid:92c93d21-c69b-4c06-9d3c-8b72e0aa5a05EnglishSymplectic ElementsSpringer Nature2019Davies, KEChamberlain, JSAn engineered truncated gene derived from the dystrophin-related protein (utrophin), prevents pathology without an immune response in an animal model of Duchenne muscular dystrophy (DMD) gene therapy. |
| spellingShingle | Davies, KE Chamberlain, JS Surrogate gene therapy for muscular dystrophy |
| title | Surrogate gene therapy for muscular dystrophy |
| title_full | Surrogate gene therapy for muscular dystrophy |
| title_fullStr | Surrogate gene therapy for muscular dystrophy |
| title_full_unstemmed | Surrogate gene therapy for muscular dystrophy |
| title_short | Surrogate gene therapy for muscular dystrophy |
| title_sort | surrogate gene therapy for muscular dystrophy |
| work_keys_str_mv | AT davieske surrogategenetherapyformusculardystrophy AT chamberlainjs surrogategenetherapyformusculardystrophy |