Surrogate gene therapy for muscular dystrophy
An engineered truncated gene derived from the dystrophin-related protein (utrophin), prevents pathology without an immune response in an animal model of Duchenne muscular dystrophy (DMD) gene therapy.
Main Authors: | Davies, KE, Chamberlain, JS |
---|---|
Format: | Journal article |
Language: | English |
Published: |
Springer Nature
2019
|
Similar Items
-
Therapeutic approaches to muscular dystrophy.
by: Goyenvalle, A, et al.
Published: (2011) -
The Pathogenesis and Therapy of Muscular Dystrophies
by: Guiraud, S, et al.
Published: (2015) -
Progress in therapy for Duchenne muscular dystrophy.
by: Fairclough, R, et al.
Published: (2011) -
Progress in therapy for Duchenne muscular dystrophy
by: Fairclough, R, et al.
Published: (2011) -
Utrophin in the therapy of Duchenne Muscular Dystrophy
by: Potter, A, et al.
Published: (2006)