Surrogate gene therapy for muscular dystrophy

An engineered truncated gene derived from the dystrophin-related protein (utrophin), prevents pathology without an immune response in an animal model of Duchenne muscular dystrophy (DMD) gene therapy.

書誌詳細
主要な著者:	Davies, KE, Chamberlain, JS
フォーマット:	Journal article
言語:	English
出版事項:	Springer Nature 2019

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