RPGR gene therapy presents challenges in cloning the coding sequence

RPGR gene therapy presents challenges in cloning the coding sequence

<p><strong>Introduction:</strong> Currently, there are three Phase I/II clinical trials based on gene therapy ongoing to test different AAV.RPGR or deleted RPGR vectors on patients affected by X-linked retinitis pigmentosa. These three vectors differ in the adeno-associated viral (...

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Những tác giả chính:	Martinez-Fernandez De La Camara, C, Cehajic-Kapetanovic, J, MacLaren, RE
Định dạng:	Journal article
Ngôn ngữ:	English
Được phát hành:	Taylor and Francis 2019

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