Acetyl-Leucine slows disease progression in lysosomal storage disorders

Bibliographic Details
Main Authors: Kaya, E, Smith, DE, Smith, C, Morris, L, Bremova-Ertl, T, Cortina-Borja, M, Fineran, P, Morten, KJ, Poulton, J, Spencer, J, Strupp, ML, Platt, F
Format: Conference item
Language:English
Published: Wiley 2020