Acetyl-Leucine slows disease progression in lysosomal storage disorders

Eitemau Tebyg

• Acetyl-Leucine slows disease progression in lysosomal storage disorders
  gan: Kaya, E, et al.
  Cyhoeddwyd: (2020)
• Beneficial effects of acetyl-DL-Leucine (ADLL) in a mouse model of Sandhoff disease
  gan: Kaya, E, et al.
  Cyhoeddwyd: (2020)
• An anecdotal report by an Oxford basic neuroscientist: effects of acetyl-dl-leucine on cognitive function and mobility in the elderly
  gan: Platt, F, et al.
  Cyhoeddwyd: (2016)
• Annual severity increment score as a tool for stratifying patients with Niemann-Pick disease type C and for recruitment to clinical trials
  gan: Cortina-Borja, M, et al.
  Cyhoeddwyd: (2018)
• A master protocol to investigate a novel therapy acetyl-L-leucine for three ultra-rare neurodegenerative diseases: Niemann-Pick type C, the GM2 gangliosidoses, and ataxia telangiectasia
  gan: Fields, T, et al.
  Cyhoeddwyd: (2021)