Developing gene knockdown-replacement therapies for spinocerebellar ataxia type 7
<p>For many dominant diseases, conventional treatment options are limited. This makes them attractive candidates for gene therapy, which may be directed to specifically silence a disease-causing allele. However, many mutations are not easily amenable to this technique, including nucleotide rep...
| Príomhchruthaitheoirí: | , |
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| Formáid: | Tráchtas |
| Teanga: | English |
| Foilsithe / Cruthaithe: |
2013
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| Ábhair: |