Subretinal timrepigene emparvovec in adult men with choroideremia: a randomized phase 3 trial

Subretinal timrepigene emparvovec in adult men with choroideremia: a randomized phase 3 trial

<p>Choroideremia is a rare, X-linked retinal degeneration resulting in progressive vision loss. A randomized, masked, phase 3 clinical trial evaluated the safety and efficacy over 12 months of follow-up in adult males with choroideremia randomized to receive a high-dose (1.0&thi...

Полное описание

Библиографические подробности
Главные авторы:	MacLaren, RE, Fischer, MD, Gow, JA, Lam, BL, Sankila, E-MK, Girach, A, Panda, S, Yoon, D, Zhao, G, Pennesi, ME
Формат:	Journal article
Язык:	English
Опубликовано:	Springer Nature 2023

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