Emerging gene therapies for cystic fibrosis
<p><strong>Introduction</strong>: Cystic fibrosis (CF) remains a life-threatening genetic disease, with few clinically effective treatment options. Gene therapy and gene editing strategies offer the potential for a one-time CF cure, irrespective of the <em>CFTR</em> mut...
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| Formato: | Journal article |
| Lenguaje: | English |
| Publicado: |
Taylor and Francis
2019
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