Potential lifetime quality of life benefits of choroideremia gene therapy: projections from a clinically informed decision model

Potential lifetime quality of life benefits of choroideremia gene therapy: projections from a clinically informed decision model

<p><strong>Background</strong> The first gene therapy for an inherited retinal dystrophy recently received market approval in the United States; multiple other gene therapies are in the clinical pipeline. Thus far, gene therapy has commanded prices in the range of USD 500,000 to ov...

書誌詳細
主要な著者:	Halioua-Haubold, C-L, Jolly, JK, Smith, JA, Villanueva, R, Brindley, DA, MacLaren, RE
フォーマット:	Journal article
出版事項:	Springer Nature 2019

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