Newborn screening for SMA in Southern Belgium
Approval was recently granted for a new treatment for spinal muscular atrophy (SMA). Given that the treatment is effective when administered early and the societal burden of SMA-related disability, the implementation of a newborn screening program is warranted. We describe the stepwise process that...
প্রধান লেখক: | Boemer, F, Caberg, J-H, Dideberg, V, Dardenne, D, Bours, V, Hiligsmann, M, Dangouloff, T, Servais, L |
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বিন্যাস: | Journal article |
ভাষা: | English |
প্রকাশিত: |
Elsevier
2019
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অনুরূপ উপাদানগুলি
অনুরূপ উপাদানগুলি
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