Newborn screening for SMA in Southern Belgium

Newborn screening for SMA in Southern Belgium

Approval was recently granted for a new treatment for spinal muscular atrophy (SMA). Given that the treatment is effective when administered early and the societal burden of SMA-related disability, the implementation of a newborn screening program is warranted. We describe the stepwise process that...

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Dades bibliogràfiques
Autors principals:	Boemer, F, Caberg, J-H, Dideberg, V, Dardenne, D, Bours, V, Hiligsmann, M, Dangouloff, T, Servais, L
Format:	Journal article
Idioma:	English
Publicat:	Elsevier 2019

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