Respiratory and upper limb function as outcome measures in ambulant and non-ambulant subjects with Duchenne muscular dystrophy: A prospective multicentre study

The field of translational research in Duchenne muscular dystrophy (DMD) has been transformed in the last decade by a number of therapeutic targets, mostly studied in ambulant patients. A paucity of studies focus on measures that capture the non-ambulant stage of the disease, and the transition betw...

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Detalles Bibliográficos
Autores principales: Ricotti, V, Selby, V, Ridout, D, Domingos, J, Decostre, V, Mayhew, A, Eagle, M, Butler, J, Guglieri, M, der Holst, MV, Jansen, M, Verschuuren, JJGM, de Groot, IJM, Niks, EH, Servais, L, Straub, V, Voit, T, Hogrel, JY, Muntoni, F
Formato: Journal article
Lenguaje:English
Publicado: Elsevier 2019