Towards extracellular vesicle based gene therapy for Huntington's disease

Towards extracellular vesicle based gene therapy for Huntington's disease

<p>Huntington's disease (HD) can be regarded as a model neurodegenerative disorder to screen potential genetic based therapeutics and their carriers. It is an autosomal dominant disorder caused by a mutation in a single gene that leads to progressive neurodegeneration caused in part by pr...

Полное описание

Библиографические подробности
Главный автор:	O'Loughlin, A
Другие авторы:	Wood, M
Формат:	Диссертация
Опубликовано:	2016
Предметы:	Neurosciences

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