Development of AAV-mediated gene therapy for autosomal recessive bestrophinopathy

<p>The bestrophinopathies are a set of inherited retinal degenerations caused by mutations in <em>BEST1</em>, and include Best vitelliform macular dystrophy (BVMD), autosomal dominant vitreoretinochoroidopathy (ADVIRC) and autosomal recessive bestrophinopathy (ARB). The correspondi...

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Autor principal: Wood, S
Altres autors: Maclaren, R
Format: Thesis
Idioma:English
Publicat: 2017
Matèries: