Towards an engineered autologous cellular therapy for RAG2 deficiency

<p>Severe combined immune deficiency (SCID) caused by RAG deficiency is a genetically-determined immune deficiency characterized by the virtual absence of adaptive immune cells. Unless treated with a hematopoietic stem cell transplantation (HSCT), RAG deficient patients succumb to severe infec...

Повний опис

Бібліографічні деталі
Автор: Gardner, CL
Інші автори: Acuto, O
Формат: Дисертація
Мова:English
Опубліковано: 2020
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