A randomized, double-blind, placebo-controlled trial of repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis
Үндсэн зохиолчид: | Alton, E, Armstrong, D, Bayfield, K, Bilton, D, Boyd, A, Cheng, S, Cunningham, S, Davies, J, Elgmati, H, Gill, D, Greening, A, Griesenbach, U, Harman, K, Higgins, T, Hyde, S, Innes, J, McGovern, M, Murray, G, Porteous, D, Saunders, C, Scheule, R, Simmonds, N, Soussi, S, Sumner-Jones, S, Waller, M |
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Формат: | Conference item |
Хэл сонгох: | English |
Хэвлэсэн: |
Wiley
2015
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Ижил төстэй зүйлс
Ижил төстэй зүйлс
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Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial
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SAFETY AND EXPRESSION OF A SINGLE DOSE OF LIPID-MEDIATED CFTR GENE THERAPY TO THE UPPER AND LOWER AIRWAYS OF PATIENTS WITH CF
-н: Davies, J, зэрэг
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Self-reactive CFTR T cells in humans: implications for gene therapy.
-н: Calcedo, R, зэрэг
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SAFETY AND EXPRESSION OF A SINGLE DOSE OF LIPID-MEDIATED CFTR GENE THERAPY TO THE UPPER AND LOWER AIRWAYS OF PATIENTS WITH CYSTIC FIBROSIS
-н: Davies, G, зэрэг
Хэвлэсэн: (2011) -
A randomised, double-blind, placebo-controlled trial of repeated nebulisation of non-viral cystic fibrosis transmembrane conductance regulator (CFTR) gene therapy in patients with cystic fibrosis
-н: Alton, EWFW, зэрэг
Хэвлэсэн: (2016)