Long-term data with idebenone on respiratory function outcomes in patients with Duchenne muscular dystrophy
Decline in respiratory function in patients with DMD starts during early teenage years and leads to early morbidity and mortality. Published evidence of efficacy for idebenone on respiratory function outcomes is currently limited to 12 months of follow-up time. Here we report data collected as retro...
Үндсэн зохиолчид: | Servais, L, Straathof, CSM, Schara, U, Klein, A, Leinonen, M, Hasham, S, Meier, T, De Waele, L, Gordish-Dressman, H, McDonald, CM, Mayer, OH, Voit, T, Mercuri, E, Buyse, GM |
---|---|
Формат: | Journal article |
Хэл сонгох: | English |
Хэвлэсэн: |
Elsevier
2019
|
Ижил төстэй зүйлс
Ижил төстэй зүйлс
-
Cholesterol metabolism is a potential therapeutic target in Duchenne muscular dystrophy
-н: Fatima Amor, зэрэг
Хэвлэсэн: (2021-06-01) -
Duchenne Muscular Dystrophy
-н: J Gordon Millichap
Хэвлэсэн: (1989-05-01) -
Increased dystrophin production with golodirsen in patients with Duchenne muscular dystrophy
-н: Frank, DE, зэрэг
Хэвлэсэн: (2020) -
Muscular Fatigue in Duchenne Dystrophy
-н: J Gordon Millichap
Хэвлэсэн: (1995-02-01) -
Glucocorticoids for Duchenne Muscular Dystrophy
-н: J Gordon Millichap
Хэвлэсэн: (2013-07-01)