The potential role of miRNA therapies in spinal muscle atrophy
Spinal muscular atrophy (SMA) is a neurodegenerative disease caused by low levels of full-length survival motor neuron (SMN) protein due to the loss of the survival motor neuron 1 (SMN1) gene and inefficient splicing of the survival motor neuron 2 (SMN2) gene, which mostly affects alpha motor neuron...
| Main Authors: | , , , |
|---|---|
| Format: | Article |
| Language: | English |
| Published: |
Elsevier BV
2021
|
| Online Access: | http://psasir.upm.edu.my/id/eprint/95562/1/The%20potential%20role%20of%20miRNA%20therapies%20in%20spinal%20muscle%20atrophy.pdf |