Oncogenic miR-27a delivered by exosomes binds to SFRP1 and promotes angiogenesis in renal clear cell carcinoma by Yi Hou, Li Fan, Hai Li

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U1 Adaptor Oligonucleotides Targeting BCL2 and GRM1 Suppress Growth of Human Melanoma Xenografts In Vivo by Rafal Goraczniak, Brian A. Wall, Mark A. Behlke, Kim A. Lennox, Eric S. Ho, Nikolas H. Zaphiros, Christopher Jakubowski, Neil R. Patel, Steven Zhao, Carlo Magaway, Stacey A. Subbie, Lumeng Jenny Yu, Stephanie LaCava, Kenneth R. Reuhl, Suzie Chen, Samuel I. Gunderson

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Long-term muscle-specific overexpression of DOK7 in mice using AAV9-tMCK-DOK7 by Yu-Ting Huang, Hannah R. Crick, Helena Chaytow, Dinja van der Hoorn, Abrar Alhindi, Ross A. Jones, Ralph D. Hector, Stuart R. Cobb, Thomas H. Gillingwater

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Reprogramming the Dynamin 2 mRNA by Spliceosome-mediated RNA Trans-splicing by Delphine Trochet, Bernard Prudhon, Arnaud Jollet, Stéphanie Lorain, Marc Bitoun

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Therapeutic and diagnostic applications of antisense peptide nucleic acids by Victoria MacLelland, Madeline Kravitz, Anisha Gupta

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Partial restoration of brain dystrophin by tricyclo-DNA antisense oligonucleotides alleviates emotional deficits in mdx52 mice by Amel Saoudi, Sacha Barberat, Olivier le Coz, Ophélie Vacca, Mathilde Doisy Caquant, Thomas Tensorer, Eric Sliwinski, Luis Garcia, Francesco Muntoni, Cyrille Vaillend, Aurélie Goyenvalle

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Antisense Oligonucleotide Therapeutic Approach for Suppression of Ataxin-1 Expression: A Safety Assessment by Brennon O’Callaghan, Bente Hofstra, Hillary P. Handler, Holly B. Kordasiewicz, Tracy Cole, Lisa Duvick, Jillian Friedrich, Orion Rainwater, Praseuth Yang, Michael Benneyworth, Tessa Nichols-Meade, Wesley Heal, Rachel Ter Haar, Christine Henzler, Harry T. Orr

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Cell-type-specific alternative polyadenylation promotes oncogenic gene expression in non-small cell lung cancer progression by Kexin Huang, Yun Zhang, Xiaorui Shi, Zhiqin Yin, Weiling Zhao, Liyu Huang, Fu Wang, Xiaobo Zhou

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Multi-gene duplication removal in an engineered human cellular MECP2 duplication syndrome model with an IRAK1-MECP2 duplication by Samar Z. Rizvi, Wing Suen Chan, Eleonora Maino, Sydney Steiman, Georgiana Forguson, Maya Klepfish, Ronald D. Cohn, Evgueni A. Ivakine

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RNA therapeutics in targeting G protein-coupled receptors: Recent advances and challenges by Wanjun Yuan, Xiangyang Shi, Leo Tsz On Lee

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Less is more: Allele-specific removal of dysfunctional RYR1 channel subunits by Derek Sun, William R. Lagor

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Lateral flow immunoassay for rapid and sensitive detection of dsRNA contaminants in in vitro-transcribed mRNA products by Dengwang Luo, Zhanfeng Wu, Daming Wang, Jieli Zhang, Fei Shao, Shuo Wang, Stefano Cestellos-Blanco, Dawei Xu, Yuhong Cao

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Editing of homologous globin genes by nickase-deficient base editor mitigates large intergenic deletions in HSPCs by Anila George, Poornasree Sadanandan, Nithin Sam Ravi, B. Vaishnavi, Srujan Marepally, Saravanbhavan Thangavel, Shaji R. Velayudhan, Alok Srivastava, Kumarasamypet M Mohankumar

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Joint masking and self-supervised strategies for inferring small molecule-miRNA associations by Zhecheng Zhou, Linlin Zhuo, Xiangzheng Fu, Juan Lv, Quan Zou, Ren Qi

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Efficient CRISPR-Cas9-mediated mutagenesis in primary human B cells for identifying plasma cell regulators by Tuan Anh Le, Van Trung Chu, Andreia C. Lino, Eva Schrezenmeier, Christopher Kressler, Dania Hamo, Klaus Rajewsky, Thomas Dörner, Van Duc Dang

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Ubiquitinated ligation protein NEDD4L participates in MiR-30a-5p attenuated atherosclerosis by regulating macrophage polarization and lipid metabolism by Fei Song, Jing-Zhou Li, Yao Wu, Wei-Yin Wu, Yan Wang, Gang Li

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Galaxy Workflows for Web-based Bioinformatics Analysis of Aptamer High-throughput Sequencing Data by William H Thiel

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704/DNA vaccines leverage cytoplasmic DNA stimulation to promote anti-HIV neutralizing antibody production in mice and strong immune response against alpha-fetoprotein in non-human... by Thibault Colombani, Thomas Haudebourg, Bruno Pitard

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Sequencing-guided design of genetically encoded small RNAs targeting CAG repeats for selective inhibition of mutant huntingtin by Mansi A. Parasrampuria, Adam A. White, Ramadevi Chilamkurthy, Adrian A. Pater, Fatima El-Azzouzi, Katy N. Ovington, Philip J. Jensik, Keith T. Gagnon

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Suppression of IGF1R in Melanoma Cells by an Adenovirus-Mediated One-Step Knockdown System by Haoran Xin, Mingxing Lei, Zhihui Zhang, Jie Li, Hao Zhang, Xinwei Luo, Aoyun Wang, Fang Deng

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