Correction to: Physiologically Based Pharmacokinetic Modeling of CFTR Modulation in People with Cystic Fibrosis Transitioning from Mono or Dual Regimens to Triple-Combination Elexa... by Alice Tsai, Shu-Pei Wu, Eric Haseltine, Sanjeev Kumar, Samuel M. Moskowitz, Paul Panorchan, Kushal Shah

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PB2508: COMPARING DEFINITIONS OF EPISODES OF VASO-OCCLUSION AS ENDPOINTS IN CLINICAL STUDIES OF SICKLE CELL DISEASE by Franco Locatelli, Nanxin LI, Suzan Imren, Fengjuan Xuan, Jaime Rubin, Bill Hobbs, Haydar Frangoul

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PB2511: CLINICAL COMPLICATIONS AMONG PATIENTS WITH SICKLE CELL DISEASE WITH RECURRENT VASO-OCCLUSIVE CRISES IN GERMANY by Chuka Udeze, Colin Kunzweiler, Nanxin LI, Jessica Baldwin, Petra Tuzin, Sebastian Dietmar Barth, Céline Vetter, Silvia Dombrowski, Elena Georgiadou-Schmidt, Roland Meisel

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P1464: CLINICAL COMPLICATIONS AMONG PATIENTS WITH TRANSFUSION-DEPENDENT BETA-THALASSEMIA IN GERMANY by Chuka Udeze, Colin Kunzweiler, Nanxin LI, Jessica Baldwin, Petra Tuzin, Sebastian Dietmar Barth, Céline Vetter, Silvia Dombrowski, Elena Georgiadou-Schmidt, Roland Meisel

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Mechanism of glycogen synthase inactivation and interaction with glycogenin by Laura Marr, Dipsikha Biswas, Leonard A. Daly, Christopher Browning, Sarah C. M. Vial, Daniel P. Maskell, Catherine Hudson, Jay A. Bertrand, John Pollard, Neil A. Ranson, Heena Khatter, Claire E. Eyers, Kei Sakamoto, Elton Zeqiraj

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P1482: PATIENTS WITH SEVERE SICKLE CELL DISEASE ON STANDARD OF CARE TREATMENT ARE VERY UNLIKELY TO BECOME VOC FREE FOR ONE YEAR: A COHORT STUDY OF MEDICAID ENROLLEES by M. Mahesri, S. B. Lee, R. Levin, S. Imren, L. Zhang, T. Beukelman, L. Titievsky, R. J. Desai

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S270: TRANSFUSION INDEPENDENCE AFTER EXAGAMGLOGENE AUTOTEMCEL IN PATIENTS WITH TRANSFUSION-DEPENDENT ΒETA-THALASSEMIA by Franco Locatelli, Peter Lang, Selim Corbacioglu, Amanda LI, Josu De La Fuente, Donna Wall, Roland Meisel, Ami J. Shah, Robert Liem, Markus Mapara, Ben Carpenter, Janet Kwiatkowski, Maria Domenica Cappellini, Antonis Kattamis, Sujit Sheth, Stephan Grupp, Puja Kohli, Daoyuan Shi, Leorah Ross, Yael Bobruff, Christopher Simard, Lanju Zhang, Phuong Khanh Morrow, Bill Hobbs, Haydar Frangoul

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Physiologically Based Pharmacokinetic Modeling of CFTR Modulation in People with Cystic Fibrosis Transitioning from Mono or Dual Regimens to Triple-Combination Elexacaftor/Tezacaft... by Alice Tsai, Shu-Pei Wu, Eric Haseltine, Sanjeev Kumar, Samuel M. Moskowitz, Paul Panorchan, Kushal Shah

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A Novel Immunophilin Ligand: Distinct Branching Effects on Dopaminergic Neurons in Culture and Neurotrophic Actions after Oral Administration in an Animal Model of Parkinson's Dise... by L.C. Costantini, P. Chaturvedi, D.M. Armistead, P.G. McCaffrey, T.W. Deacon, O. Isacson

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Clinical development of triple-combination CFTR modulators for cystic fibrosis patients with one or two F508del alleles by Jennifer L. Taylor-Cousar, Marcus A. Mall, Bonnie W. Ramsey, Edward F. McKone, Elizabeth Tullis, Gautham Marigowda, Charlotte M. McKee, David Waltz, Samuel M. Moskowitz, Jessica Savage, Fengjuan Xuan, Steven M. Rowe

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P1452: MORTALITY AND CLINICAL COMPLICATIONS AMONG PATIENTS WITH TRANSFUSION-DEPENDENT BETA-THALASSEMIA IN ITALY by Chuka Udeze, Melanie Dovizio, Chiara Veronesi, Luca Degli Esposti, Nanxin LI, Thi Xuan Mai Patricia Dang, Gian Luca Forni

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P1447: MORTALITY AND CLINICAL COMPLICATIONS AMONG PATIENTS WITH SICKLE CELL DISEASE WITH RECURRENT VASO-OCCLUSIVE CRISES IN ITALY by Chuka Udeze, Melanie Dovizio, Chiara Veronesi, Luca Degli Esposti, Nanxin LI, Thi Xuan Mai Patricia Dang, Gian Luca Forni

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P1704: PROJECTED LIFETIME ECONOMIC BURDEN OF SEVERE SICKLE CELL DISEASE IN THE UNITED STATES by C. Udeze, K. Maruszczyk, M. Atter, A. Lopez

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Impact of Elexacaftor/Tezacaftor/Ivacaftor on Healthcare Resource Utilization and Associated Costs Among People With Cystic Fibrosis in the US: A Retrospective Claims Analysis by Michael S. Schechter, Natalia Sabater-Anaya, Gerry Oster, Derek Weycker, Hongsheng Wu, Emilio Arteaga-Solis, Sukirti Bagal, Lisa J. McGarry, Kate Van Brunt, Jessica Morlando Geiger

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PB2339: PROJECTED LIFETIME ECONOMIC BURDEN OF TRANSFUSION DEPENDENT BETA-THALASSEMIA IN THE UNITED STATES by C. Udeze, K. Maruszczyk, M. Atter, A. Lopez

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P1703: ECONOMIC BURDEN OF TRANSFUSION-DEPENDENT BETA-THALASSEMIA IN THE UNITED STATES by C. Udeze, R. McKenna, Y. Yang, K. Evans, P. Smith, B. Andemariam

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Prediction of the changes in drug dissolution from an immediate-release tablet containing two active pharmaceutical ingredients using an accelerated stability assessment program (A... by Hanlin Li, David Nadig, Andrew Kuzmission, Christopher M. Riley

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A signature for immune response correlates with HCV treatment outcome in Caucasian subjects by Brian J. Hare, Eric Haseltine, Mark Fleming, Daniel Chelsky, Laura McIntosh, Rene Allard, Martyn Botfield

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Deletion of the MAD2L1 spindle assembly checkpoint gene is tolerated in mouse models of acute T-cell lymphoma and hepatocellular carcinoma by Floris Foijer, Lee A Albacker, Bjorn Bakker, Diana C Spierings, Ying Yue, Stephanie Z Xie, Stephanie Davis, Annegret Lutum-Jehle, Darin Takemoto, Brian Hare, Brinley Furey, Roderick T Bronson, Peter M Lansdorp, Allan Bradley, Peter K Sorger

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Long-Term Ivacaftor in People Aged 6 Years and Older with Cystic Fibrosis with Ivacaftor-Responsive Mutations by Joseph M. Pilewski, Kris De Boeck, Jerry A. Nick, Simon Tian, Cynthia DeSouza, Mark Higgins, Richard B. Moss

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