Stem Cell Therapies for Epidermolysis Bullosa Treatment by Argyrw Niti, Georgios Koliakos, Anna Michopoulou

Subjects: Get full text

Myeloid cell‐based delivery of IFN‐γ reprograms the leukemia microenvironment and induces anti‐tumoral immune responses by Adele Mucci, Gabriele Antonarelli, Carolina Caserta, Francesco Maria Vittoria, Giacomo Desantis, Riccardo Pagani, Beatrice Greco, Monica Casucci, Giulia Escobar, Laura Passerini, Nico Lachmann, Francesca Sanvito, Matteo Barcella, Ivan Merelli, Luigi Naldini, Bernhard Gentner

Subjects: “…ex vivo gene therapy…”
Get full text

Hematopoietic stem cell gene therapy ameliorates CNS involvement in murine model of GM1-gangliosidosis by Toshiki Tsunogai, Toya Ohashi, Yohta Shimada, Takashi Higuchi, Ayaka Kimura, Ayako M. Watabe, Fusao Kato, Hiroyuki Ida, Hiroshi Kobayashi

Subjects: Get full text

First-in-human autologous implantation of genetically modified adipocytes expressing LCAT for the treatment of familial LCAT deficiency by Masayuki Aso, Tokuo T. Yamamoto, Masayuki Kuroda, Jun Wada, Yoshitaka Kubota, Ko Ishikawa, Yoshiro Maezawa, Naoya Teramoto, Ayako Tawada, Sakiyo Asada, Yasuyuki Aoyagi, Mika Kirinashizawa, Akinobu Onitake, Yuta Matsuura, Kunio Yasunaga, Shun-ichi Konno, Katsuaki Nishino, Misato Yamamoto, Junko Miyoshi, Norihiko Kobayashi, Masami Tanio, Takayuki Ikeuchi, Hidetoshi Igari, Nobuyuki Mitsukawa, Hideki Hanaoka, Koutaro Yokote, Yasushi Saito

Subjects: Get full text

LCAT-trial-24 weeks: Protocol for a clinical study to evaluate the safety of regenerative medicine and gene therapy by the autologous transplantation of human lecithin:cholesterol... by Masayuki Kuroda, Makoto Hori, Yoshiro Maezawa, Yoshitaka Kubota, Nobuyuki Mitsukawa, Yuki Shiko, Yoshihito Ozawa, Yohei Kawasaki, Yasushi Saito, Hideki Hanaoka, Koutaro Yokote

Subjects: Get full text

Ex Vivo Gene Therapy Treats Bone Complications of Mucopolysaccharidosis Type II Mouse Models through Bone Remodeling Reactivation by Miho Wada, Yohta Shimada, Sayoko Iizuka, Natsumi Ishii, Hiromi Hiraki, Toshiaki Tachibana, Kazuhiro Maeda, Mitsuru Saito, Shoutaro Arakawa, Takuya Ishimoto, Takayoshi Nakano, Hiroyuki Ida, Toya Ohashi, Hiroshi Kobayashi

Subjects: Get full text

CRISPR-Cas9 Gene Editing of Hematopoietic Stem Cells from Patients with Friedreich’s Ataxia by Celine J. Rocca, Joseph N. Rainaldi, Jay Sharma, Yanmeng Shi, Joseph H. Haquang, Jens Luebeck, Prashant Mali, Stephanie Cherqui

Subjects: Get full text

Long-Term PEDF Release in Rat Iris and Retinal Epithelial Cells after Sleeping Beauty Transposon-Mediated Gene Delivery by Laura Garcia-Garcia, Sergio Recalde, Maria Hernandez, Jaione Bezunartea, Juan Roberto Rodriguez-Madoz, Sandra Johnen, Sabine Diarra, Corinne Marie, Zsuzsanna Izsvák, Zoltán Ivics, Daniel Scherman, Martina Kropp, Gabriele Thumann, Felipe Prosper, Patricia Fernandez-Robredo, Alfredo Garcia-Layana

Subjects: Get full text

Gene-modified leucoconcentrate for personalized ex vivo gene therapy in a mini pig model of moderate spinal cord injury by Rustem R Islamov, Farid V Bashirov, Mikhail E Sokolov, Andrei A Izmailov, Filip O Fadeev, Vage A Markosyan, Maria A Davleeva, Olga V Zubkova, Maxim M Smarov, Denis Yu Logunov, Boris S Naroditskyi, Ilnur I Salafutdinov, Albert A Rizvanov, Ramil G Turaev

Subjects: “…chimeric ad5/35f virus; enhanced green fluorescent protein; gene-modified leucoconcentrate; mini pig; peripheral blood; personalized ex vivo gene therapy; plastic blood bag; spinal cord injury…”
Get full text