Elosulfase alfa in the treatment of mucopolysaccharidosis type IVA: insights from the first managed access agreement by Bob Stevens, Tom Kenny, Sophie Thomas, Alexandra Morrison, James Jarrett, Mohit Jain

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Mucopolysaccharidosis type IVA in children: Clinical cases by A. V. Burlutskaya, N. V. Savel′eva, G. V. Naumenko

Subjects: “…mucopolysaccharidosis type iva…”
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Clinical characteristics and effects of enzyme replacement therapy with elosulfase alfa in Korean patients with mucopolysaccharidosis type IVA by Seung Hoon Lee, Hwa Young Kim, Tae-Joon Cho, Hyoungmin Kim, Jung Min Ko

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Oxidative profile exhibited by Mucopolysaccharidosis type IVA patients at diagnosis: Increased keratan urinary levels by Bruna Donida, Desirèe P. Marchetti, Carlos Eduardo Diaz Jacques, Graziela Ribas, Marion Deon, Paula Manini, Helen Tais da Rosa, Dinara Jaqueline Moura, Jenifer Saffi, Roberto Giugliani, Carmen Regla Vargas

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Adeno-associated virus-based gene therapy delivering combinations of two growth-associated genes to MPS IVA mice by Estera Rintz, Betul Celik, Nidhi Fnu, Angélica María Herreño-Pachón, Shaukat Khan, Eliana Benincore-Flórez, Shunji Tomatsu

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Clinical Characteristics of a Patient with Mucopolysaccharidosis Type IVA (Morquio Syndrome) by Nato D. Vashakmadze, Natalia V. Zhurkova, Ludmila K. Mikhaylova, Volha Ya. Smirnova, Grigorii V. Revunenkov

Subjects: “…mucopolysaccharidosis type iva…”
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