Dornase alfa in Cystic Fibrosis: indications, comparative studies and effects on lung clearance index

Abstract Cystic fibrosis (CF) is the most common inherited disease in Caucasian populations, affecting around 50,000 patients in Europe and 30,000 in United States. A mutation in CF trans-membrane conductance regulator (CFTR) gene changes a protein (a regulated chloride channel), which is expressed...

Full description

Bibliographic Details
Main Authors: Vito Terlizzi, Chiara Castellani, Giovanni Taccetti, Beatrice Ferrari
Format: Article
Language:English
Published: BMC 2022-08-01
Series:Italian Journal of Pediatrics
Subjects:
Online Access:https://doi.org/10.1186/s13052-022-01331-5