Dornase alfa in Cystic Fibrosis: indications, comparative studies and effects on lung clearance index
Abstract Cystic fibrosis (CF) is the most common inherited disease in Caucasian populations, affecting around 50,000 patients in Europe and 30,000 in United States. A mutation in CF trans-membrane conductance regulator (CFTR) gene changes a protein (a regulated chloride channel), which is expressed...
Main Authors: | , , , |
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Format: | Article |
Language: | English |
Published: |
BMC
2022-08-01
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Series: | Italian Journal of Pediatrics |
Subjects: | |
Online Access: | https://doi.org/10.1186/s13052-022-01331-5 |