Trikafta—Extending Its Success to Less Common Mutations

Cystic Fibrosis (a genetic recessive disease) is caused by a mutant cystic fibrosis transmembrane conductance regulator (CFTR) gene that causes an absence of, or impaired CFTR activity [...]

Bibliographic Details
Main Authors: Lea Bentur, Mordechai Pollak
Format: Article
Language:English
Published: MDPI AG 2022-09-01
Series:Journal of Personalized Medicine
Subjects:
n/a
Online Access:https://www.mdpi.com/2075-4426/12/9/1528