Trikafta—Extending Its Success to Less Common Mutations
Cystic Fibrosis (a genetic recessive disease) is caused by a mutant cystic fibrosis transmembrane conductance regulator (CFTR) gene that causes an absence of, or impaired CFTR activity [...]
Main Authors: | , |
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Format: | Article |
Language: | English |
Published: |
MDPI AG
2022-09-01
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Series: | Journal of Personalized Medicine |
Subjects: | |
Online Access: | https://www.mdpi.com/2075-4426/12/9/1528 |