The potential impact of gene therapy on health-related quality of life (HRQoL) domains in haemophilia

The potential impact of gene therapy on health-related quality of life (HRQoL) domains in haemophilia

Haemophilia is an inherited bleeding disorder characterised by spontaneous bleeding, often leading to impaired health-related quality of life (HRQoL). Commonly used treatments include episodic and prophylactic treatment regimens. Gene therapies could soon become available, potentially creating a par...

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Bibliographic Details
Main Authors: Bullinger Monika, Gardner Diandra Latibeaudiere, Lewis Hannah B, Miesbach Wolfgang, Nolte Sandra, O’Hara Jamie, O’Mahony Brian, Pollard Debra, Skinner Mark, Quinn Jennifer
Format: Article
Language:English
Published: Sciendo 2021-05-01
Series:The Journal of Haemophilia Practice
Subjects:
haemophilia
gene therapy
patient-reported outcomes
health-related quality of life
Online Access:https://doi.org/10.17225/jhp00176

Internet

https://doi.org/10.17225/jhp00176

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