Bilateral exudative retinal detachments after subretinal gene therapy with voretigene neparvovec-rzyl for RPE65 Leber Congenital Amaurosis

Bilateral exudative retinal detachments after subretinal gene therapy with voretigene neparvovec-rzyl for RPE65 Leber Congenital Amaurosis

Purpose: To report panuveitis with exudative retinal detachments in a healthy 27-year-old woman with biallelic mutations in the RPE65 gene, who underwent bilateral sequential gene therapy with subretinal administration of voretigene neparvovec-rzyl. Observations: Visual acuity improved for 30 days a...

Podrobná bibliografie
Hlavní autoři:	Alcina K. Lidder, Stephanie Choi, Yasha S. Modi, Scott E. Brodie, Janet L. Davis, Ninel Z. Gregori, Byron L. Lam
Médium:	Článek
Jazyk:	English
Vydáno:	Elsevier 2023-12-01
Edice:	American Journal of Ophthalmology Case Reports
Témata:	Subretinal gene therapy Leber congenital amaurosis Vogt-koyanagi-harada disease Sympathetic ophthalmia RPE65-Associated inherited retinal disease Panuveitis
On-line přístup:	http://www.sciencedirect.com/science/article/pii/S2451993623000877

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