Determining value in the treatment of activated PI3Kδ syndrome in Spain: a multicriteria decision analysis from the perspective of key stakeholders

Introduction: Activated phosphoinositide 3-kinase (PI3K)δ syndrome (APDS) is an ultra-rare inborn error of immunity (IEI) combining immunodeficiency and immune dysregulation. This study determined what represents value in APDS in Spain from a multidisciplinary perspective applying multicriteria deci...

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Bibliographic Details
Main Authors: Alicia Gil, María Reyes Abad, Carmen Alerany, Laia Alsina, Eduardo López Granados, Olaf Neth, José Luis Poveda, Jacques G. Rivière, Carlos Rodríguez-Gallego, Joanne B. Tutein Nolthenius, Raquel Figueiredo, Silvia Subías Labazuy
Format: Article
Language:English
Published: AboutScience Srl 2024-05-01
Series:Global & Regional Health Technology Assessment
Subjects:
Online Access:https://journals.aboutscience.eu/index.php/grhta/article/view/3041