O07: Optimization of positive investigational outcomes in Barth syndrome using a combination of placebo-controlled, extended open-label, and natural history comparison studies*

Bibliographic Details
Main Authors:	Hilary Vernon, Brittany Hornby, Anthony Abbruscato, Jim Carr, W. Reid Thompson
Format:	Article
Language:	English
Published:	Elsevier 2023-01-01
Series:	Genetics in Medicine Open
Online Access:	http://www.sciencedirect.com/science/article/pii/S2949774423000080

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