Social pharmaceutical innovation and alternative forms of research, development and deployment for drugs for rare diseases

Abstract Rare diseases are associated with difficulties in addressing unmet medical needs, lack of access to treatment, high prices, evidentiary mismatch, equity, etc. While challenges facing the development of drugs for rare diseases are experienced differently globally (i.e., higher vs. lower and...

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Détails bibliographiques
Auteurs principaux: Conor M. W. Douglas, Fernando Aith, Wouter Boon, Marina de Neiva Borba, Liliana Doganova, Shir Grunebaum, Rob Hagendijk, Larry Lynd, Alexandre Mallard, Faisal Ali Mohamed, Ellen Moors, Claudio Cordovil Oliveira, Florence Paterson, Vanessa Scanga, Julino Soares, Vololona Raberharisoa, Tineke Kleinhout-Vliek
Format: Article
Langue:English
Publié: BMC 2022-09-01
Collection:Orphanet Journal of Rare Diseases
Sujets:
Accès en ligne:https://doi.org/10.1186/s13023-022-02476-6