Educational needs of patients, families, and healthcare professionals to support the patient journey in haemophilia gene therapy in the UK

Educational needs of patients, families, and healthcare professionals to support the patient journey in haemophilia gene therapy in the UK

Abstract With the first gene therapies for haemophilia approved by the European Commission, the US Food and Drug Administration, and the Medicines and Healthcare products Regulatory Agency, it is important to consider the remaining unmet needs and challenges that may arise throughout patients’ treat...

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Bibliographic Details
Main Authors: Sara Boyce, Simon Fletcher, April Jones, Ruchika Kohli, Sarah Mangles, Min Ong, Debra Pollard, Sujan Sivasubramaniyam, David Stephensen, Nicola Stoner, Rashid Kazmi
Format: Article
Language:English
Published: BMC 2023-11-01
Series:Orphanet Journal of Rare Diseases
Subjects:
Gene therapy
Haemophilia A
Haemophilia B
Health services needs and demand
Patient navigation
Online Access:https://doi.org/10.1186/s13023-023-02977-y

Internet

https://doi.org/10.1186/s13023-023-02977-y

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