Diagnosis and Emerging Treatment Strategies for Mucopolysaccharidosis VII (Sly Syndrome)

Diagnosis and Emerging Treatment Strategies for Mucopolysaccharidosis VII (Sly Syndrome)

Fabiano de Oliveira Poswar,1– 4 Johanna Henriques Nehm,1 Francyne Kubaski,5 Edina Poletto,6 Roberto Giugliani1– 4,7– 9 1Clinical Research Group in Medical Genetics, Clinical Research Center, Hospital de Clínicas de Porto Alegre, Porto Alegre, RS, Brazil; 2Medical Genetics Service, Hospital de Clinic...

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Bibliographic Details
Main Authors: Poswar FDO, Henriques Nehm J, Kubaski F, Poletto E, Giugliani R
Format: Article
Language:English
Published: Dove Medical Press 2022-12-01
Series:Therapeutics and Clinical Risk Management
Subjects:
lysosomal disorders
mucopolysaccharidosis type vii
sly syndrome
enzyme replacement therapy
hematopoietic stem cell transplantation
gene therapy.
Online Access:https://www.dovepress.com/diagnosis-and-emerging-treatment-strategies-for-mucopolysaccharidosis--peer-reviewed-fulltext-article-TCRM

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https://www.dovepress.com/diagnosis-and-emerging-treatment-strategies-for-mucopolysaccharidosis--peer-reviewed-fulltext-article-TCRM

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