The effect of intravenous trehalose administration in a patient with multiple sulfatase deficiency
Introduction We describe the case of a female child with multiple sulfatase deficiency (MSD) who received intravenous (IV) trehalose (15 g/week) for 3 months. Material and methods The efficacy of trehalose was evaluated by comparing serum biomarkers, a quality-of-life questionnaire (HRQoL), and ima...
Main Authors: | , , , , , |
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Format: | Article |
Language: | English |
Published: |
Termedia Publishing House
2023-01-01
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Series: | Archives of Medical Science |
Subjects: | |
Online Access: | https://www.archivesofmedicalscience.com/The-effect-of-intravenous-trehalose-administration-in-a-patient-with-multiple-sulfatase,159711,0,2.html |