DEVELOPMENT OF THE ACCURATE SPINOCEREBELLAR ATAXIA TYPE3 (SCA3) THERAPEUTICS USING EN-CAS12A NICKASE-BASED GENOME EDITING

Bibliographic Details
Main Authors: Lee Wha Gwon, Junghyung Park, Jinyoung Won, Jae-Won Huh, Youngjeon Lee, Seung Hwan Lee
Format: Article
Language:English
Published: Elsevier 2023-10-01
Series:IBRO Neuroscience Reports
Online Access:http://www.sciencedirect.com/science/article/pii/S2667242123003317