DEVELOPMENT OF THE ACCURATE SPINOCEREBELLAR ATAXIA TYPE3 (SCA3) THERAPEUTICS USING EN-CAS12A NICKASE-BASED GENOME EDITING
Main Authors: | , , , , , |
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Format: | Article |
Language: | English |
Published: |
Elsevier
2023-10-01
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Series: | IBRO Neuroscience Reports |
Online Access: | http://www.sciencedirect.com/science/article/pii/S2667242123003317 |