Multi-stakeholder sessions on major innovation topics in rare disease clinical trials

Multi-stakeholder sessions on major innovation topics in rare disease clinical trials

Abstract Background The European Joint Programme on Rare Diseases aims to enhance the rare diseases research ecosystem by bringing together stakeholders such as research funders, institutions and patient organizations. Work Package 20 focuses on the validation, use and development of innovative meth...

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Bibliographic Details
Main Authors: Daniel Bodden, Stefanie Schoenen, Stephanie Wied, Johan Verbeeck, Maya Dirani, Hiba Abou Daya, Nicole Heussen, Geert Molenberghs, Ralf-Dieter Hilgers, Rima Nabbout
Format: Article
Language:English
Published: BMC 2024-12-01
Series:Orphanet Journal of Rare Diseases
Subjects:
Finite populations
Natural history
Randomization
Multiple endpoints
Educational system
Online Access:https://doi.org/10.1186/s13023-024-03482-6

Internet

https://doi.org/10.1186/s13023-024-03482-6

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