New insights in efficacy of different ERT dosages in Fabry disease: Switch and switch-back studies data following agalsidase beta shortage. Update of systematic review

In 2016, a systematic review and a meta-analysis of existing data on the effects of switch from agalsidase beta to alfa in patients with Fabry disease showed that the switch was well tolerated and associated with stable disease progression. However, additional evidence that supports the need for an...

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Bibliographic Details
Main Authors: Eleonora Riccio, Carlo Garofalo, Ivana Capuano, Pasquale Buonanno, Guido Iaccarino, Teodolinda Di Risi, Massimo Imbriaco, Federica Riccio Cuomo, Antonio Pisani
Format: Article
Language:English
Published: Elsevier 2023-01-01
Series:Genetics in Medicine Open
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Online Access:http://www.sciencedirect.com/science/article/pii/S2949774423008142