CRISPR-Cas9-directed gene therapy for spinocerebellar ataxia type 1

Bibliographic Details
Main Authors: Mihai Miclăuș, Gabriel Balmus
Format: Article
Language:English
Published: Elsevier 2024-12-01
Series:Molecular Therapy: Nucleic Acids
Online Access:http://www.sciencedirect.com/science/article/pii/S2162253124002646