Real-world use of orphan medicinal products (OMPs) in rare disease (RD) patients: A population-based registry study

Real-world use of orphan medicinal products (OMPs) in rare disease (RD) patients: A population-based registry study

Background: Despite calls for the use of real-world data, the rare diseases (RD) treatment landscape suffers from a scarcity of data referred to orphan medicinal products (OMP) use at the population level.Objectives: We aim to describe the characteristics and patterns of utilization of OMP in a siza...

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Bibliographic Details
Main Authors: Monica Mazzucato, Cinzia Minichiello, Andrea Vianello, Laura Visonà dalla Pozza, Ema Toto, Paola Facchin
Format: Article
Language:English
Published: Frontiers Media S.A. 2022-09-01
Series:Frontiers in Pharmacology
Subjects:
orphan drugs
rare diseases
population-based registry
real-world data
prescriptions
Online Access:https://www.frontiersin.org/articles/10.3389/fphar.2022.940010/full

Internet

https://www.frontiersin.org/articles/10.3389/fphar.2022.940010/full

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