Transthyretin Amyloidosis: Update on the Clinical Spectrum, Pathogenesis, and Disease-Modifying Therapies

Abstract ATTR amyloidosis is caused by systemic deposition of transthyretin (TTR) and comprises ATTRwt (wt for wild-type) amyloidosis, ATTRv (v for variant) amyloidosis, and acquired ATTR amyloidosis after domino liver transplantation. ATTRwt amyloidosis has classically been regarded as cardiomyopat...

Full description

Bibliographic Details
Main Authors: Haruki Koike, Masahisa Katsuno
Format: Article
Language:English
Published: Adis, Springer Healthcare 2020-09-01
Series:Neurology and Therapy
Subjects:
Online Access:https://doi.org/10.1007/s40120-020-00210-7